Researchers Find Gene Therapy Can Cure Bubble Boy Disease in Babies



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The researchers have successfully treated several babies with severe combined immunodeficiency (XID-SCID-X1), a condition that causes babies to be born without an active immune system, commonly known as "Bubble Boy Disease".

The research team developed a lentiviral vector, based on HIV, to transfer a correct copy of the defective gene at the origin of the disease into the bone marrow stem …

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